On Sale in Two Years, a Simple Powder to Beat 2,400 Genetic Diseases
Daily Mail › September 15, 2008
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Summary
A POWDERED drug which eases the symptoms of incurable genetic diseases could be on sale within two years, researchers say.
They hope it could treat 2,400 conditions, including some types of cystic fibrosis and Duchenne muscular dystrophy, as well as the blood clotting disease haemophilia.See the full content of this document
Extract
On Sale in Two Years, a Simple Powder to Beat 2,400 Genetic Diseases
Many inherited diseases are caused by mutations in genes which stop cells from making vital proteins. The new drug - known only as PTC124 - makes cells less sensitive to these mutations.
Given early enough, PTC124 could even halt the progress of...See the full content of this document
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